Global Gene Therapy for Mucopolysaccharidosis Market Size, Status and Forecast 2019-2025

Published On: Jun 2019

Format: PDF

Publisher: QY Research

Pages: 91

Report ID: 1966

Mucopolysaccharidosis consists of a group of more than 40 genetic disorders that forms a part of lysosomal storage disease. They are caused by an inherited deficiency of an enzyme involved in the degradation of acid glycosaminoglycans (GAGs), which was previously known as mucopolysaccharidosis. All of the mucopolysaccharidoses are rare, autosomal recessive, except for mucopolysaccharidosis III, as it is X-linked.
Over the past few years, gene therapy has emerged as one of the most exciting approaches for the treatment of mucopolysaccharidosis. One of the promising therapy is replacement gene therapy, which replaces faulty genes with normal ones in the body. It is considered to be a potential cure to mucopolysaccharidoses and a promising option in the long run.
In 2018, the global Gene Therapy for Mucopolysaccharidosis market size was xx million US$ and it is expected to reach xx million US$ by the end of 2025, with a CAGR of xx% during 2019-2025.

This report focuses on the global Gene Therapy for Mucopolysaccharidosis status, future forecast, growth opportunity, key market and key players. The study objectives are to present the Gene Therapy for Mucopolysaccharidosis development in United States, Europe and China.

The key players covered in this study
Sangamo Therapeutics
Swedish Orphan Biovitrum
uniQure
...

Market segment by Type, the product can be split into
Intravenous
ICV
Intracerebral
Intracisternal

Market segment by Application, split into
Mucopolysaccharidosis I
Mucopolysaccharidosis II
Mucopolysaccharidosis III A
Mucopolysaccharidosis III B

Market segment by Regions/Countries, this report covers
United States
Europe
China
Japan
Southeast Asia
India
Central & South America

The study objectives of this report are:
To analyze global Gene Therapy for Mucopolysaccharidosis status, future forecast, growth opportunity, key market and key players.
To present the Gene Therapy for Mucopolysaccharidosis development in United States, Europe and China.
To strategically profile the key players and comprehensively analyze their development plan and strategies.
To define, describe and forecast the market by product type, market and key regions.

In this study, the years considered to estimate the market size of Gene Therapy for Mucopolysaccharidosis are as follows:
History Year: 2014-2018
Base Year: 2018
Estimated Year: 2019
Forecast Year 2019 to 2025
For the data information by region, company, type and application, 2018 is considered as the base year. Whenever data information was unavailable for the base year, the prior year has been considered.

Table of Contents

1 Report Overview
1.1 Study Scope
1.2 Key Market Segments
1.3 Players Covered
1.4 Market Analysis by Type
1.4.1 Global Gene Therapy for Mucopolysaccharidosis Market Size Growth Rate by Type (2014-2025)
1.4.2 Intravenous
1.4.3 ICV
1.4.4 Intracerebral
1.4.5 Intracisternal
1.5 Market by Application
1.5.1 Global Gene Therapy for Mucopolysaccharidosis Market Share by Application (2014-2025)
1.5.2 Mucopolysaccharidosis I
1.5.3 Mucopolysaccharidosis II
1.5.4 Mucopolysaccharidosis III A
1.5.5 Mucopolysaccharidosis III B
1.6 Study Objectives
1.7 Years Considered

2 Global Growth Trends
2.1 Gene Therapy for Mucopolysaccharidosis Market Size
2.2 Gene Therapy for Mucopolysaccharidosis Growth Trends by Regions
2.2.1 Gene Therapy for Mucopolysaccharidosis Market Size by Regions (2014-2025)
2.2.2 Gene Therapy for Mucopolysaccharidosis Market Share by Regions (2014-2019)
2.3 Industry Trends
2.3.1 Market Top Trends
2.3.2 Market Drivers
2.3.3 Market Opportunities

3 Market Share by Key Players
3.1 Gene Therapy for Mucopolysaccharidosis Market Size by Manufacturers
3.1.1 Global Gene Therapy for Mucopolysaccharidosis Revenue by Manufacturers (2014-2019)
3.1.2 Global Gene Therapy for Mucopolysaccharidosis Revenue Market Share by Manufacturers (2014-2019)
3.1.3 Global Gene Therapy for Mucopolysaccharidosis Market Concentration Ratio (CR5 and HHI)
3.2 Gene Therapy for Mucopolysaccharidosis Key Players Head office and Area Served
3.3 Key Players Gene Therapy for Mucopolysaccharidosis Product/Solution/Service
3.4 Date of Enter into Gene Therapy for Mucopolysaccharidosis Market
3.5 Mergers & Acquisitions, Expansion Plans

4 Breakdown Data by Type and Application
4.1 Global Gene Therapy for Mucopolysaccharidosis Market Size by Type (2014-2019)
4.2 Global Gene Therapy for Mucopolysaccharidosis Market Size by Application (2014-2019)

5 United States
5.1 United States Gene Therapy for Mucopolysaccharidosis Market Size (2014-2019)
5.2 Gene Therapy for Mucopolysaccharidosis Key Players in United States
5.3 United States Gene Therapy for Mucopolysaccharidosis Market Size by Type
5.4 United States Gene Therapy for Mucopolysaccharidosis Market Size by Application

6 Europe
6.1 Europe Gene Therapy for Mucopolysaccharidosis Market Size (2014-2019)
6.2 Gene Therapy for Mucopolysaccharidosis Key Players in Europe
6.3 Europe Gene Therapy for Mucopolysaccharidosis Market Size by Type
6.4 Europe Gene Therapy for Mucopolysaccharidosis Market Size by Application

7 China
7.1 China Gene Therapy for Mucopolysaccharidosis Market Size (2014-2019)
7.2 Gene Therapy for Mucopolysaccharidosis Key Players in China
7.3 China Gene Therapy for Mucopolysaccharidosis Market Size by Type
7.4 China Gene Therapy for Mucopolysaccharidosis Market Size by Application

8 Japan
8.1 Japan Gene Therapy for Mucopolysaccharidosis Market Size (2014-2019)
8.2 Gene Therapy for Mucopolysaccharidosis Key Players in Japan
8.3 Japan Gene Therapy for Mucopolysaccharidosis Market Size by Type
8.4 Japan Gene Therapy for Mucopolysaccharidosis Market Size by Application

9 Southeast Asia
9.1 Southeast Asia Gene Therapy for Mucopolysaccharidosis Market Size (2014-2019)
9.2 Gene Therapy for Mucopolysaccharidosis Key Players in Southeast Asia
9.3 Southeast Asia Gene Therapy for Mucopolysaccharidosis Market Size by Type
9.4 Southeast Asia Gene Therapy for Mucopolysaccharidosis Market Size by Application

10 India
10.1 India Gene Therapy for Mucopolysaccharidosis Market Size (2014-2019)
10.2 Gene Therapy for Mucopolysaccharidosis Key Players in India
10.3 India Gene Therapy for Mucopolysaccharidosis Market Size by Type
10.4 India Gene Therapy for Mucopolysaccharidosis Market Size by Application

11 Central & South America
11.1 Central & South America Gene Therapy for Mucopolysaccharidosis Market Size (2014-2019)
11.2 Gene Therapy for Mucopolysaccharidosis Key Players in Central & South America
11.3 Central & South America Gene Therapy for Mucopolysaccharidosis Market Size by Type
11.4 Central & South America Gene Therapy for Mucopolysaccharidosis Market Size by Application

12 International Players Profiles
12.1 Sangamo Therapeutics
12.1.1 Sangamo Therapeutics Company Details
12.1.2 Company Description and Business Overview
12.1.3 Gene Therapy for Mucopolysaccharidosis Introduction
12.1.4 Sangamo Therapeutics Revenue in Gene Therapy for Mucopolysaccharidosis Business (2014-2019)
12.1.5 Sangamo Therapeutics Recent Development
12.2 Swedish Orphan Biovitrum
12.2.1 Swedish Orphan Biovitrum Company Details
12.2.2 Company Description and Business Overview
12.2.3 Gene Therapy for Mucopolysaccharidosis Introduction
12.2.4 Swedish Orphan Biovitrum Revenue in Gene Therapy for Mucopolysaccharidosis Business (2014-2019)
12.2.5 Swedish Orphan Biovitrum Recent Development
12.3 uniQure
12.3.1 uniQure Company Details
12.3.2 Company Description and Business Overview
12.3.3 Gene Therapy for Mucopolysaccharidosis Introduction
12.3.4 uniQure Revenue in Gene Therapy for Mucopolysaccharidosis Business (2014-2019)
12.3.5 uniQure Recent Development

13 Market Forecast 2019-2025
13.1 Market Size Forecast by Regions
13.2 United States
13.3 Europe
13.4 China
13.5 Japan
13.6 Southeast Asia
13.7 India
13.8 Central & South America
13.9 Market Size Forecast by Product (2019-2025)
13.10 Market Size Forecast by Application (2019-2025)

14 Analyst's Viewpoints/Conclusions

15 Appendix
15.1 Research Methodology
15.1.1 Methodology/Research Approach
15.1.1.1 Research Programs/Design
15.1.1.2 Market Size Estimation
12.1.1.3 Market Breakdown and Data Triangulation
15.1.2 Data Source
15.1.2.1 Secondary Sources
15.1.2.2 Primary Sources
15.2 Disclaimer
15.3 Author Details